Gene editing provides new perspectives for humanity and science, revealing the potential to combat inherited diseases that can lead to irreversible blindness.
One such disease is Best’s disease, caused by multiple mutations in the BEST1 gene, which affects the visual organs.
New scientific discoveries published in the American Journal of Human Genetics show that replacing mutated genes may be the key to solving this problem.
Scientists suggest that replacing mutated genes using patient stem cells may have a positive effect on treatment outcome.
Gene editing techniques such as CRISPR-Cas9 have overcome some of the limitations, and gene therapy has improved vision function.
This dual approach to gene therapy has the potential to revolutionize the treatment of Best’s disease and the prevention of blindness.
